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Showing results for ISSN matching 2329-0501

Generation of X-CGD cells for vector evaluation from healthy donor CD34+ HSCs by shRNA-mediated knock down of gp91phox

JOURNAL ARTICLE published 2014 in Molecular Therapy - Methods & Clinical Development

Authors: Christian Brendel | Kerstin B Kaufmann | Anja Krattenmacher | Shweta Pahujani | Manuel Grez

https://doi.org/10.1038/mtm.2014.37 Actions

Detection of Replication Competent Lentivirus Using a qPCR Assay for VSV-G

JOURNAL ARTICLE published June 2018 in Molecular Therapy - Methods & Clinical Development

Authors: Lindsey M. Skrdlant | Randall J. Armstrong | Brett M. Keidaisch | Mario F. Lorente | David L. DiGiusto

https://doi.org/10.1016/j.omtm.2018.02.007 Actions

Development of a real-time imaging system for hypoxic cell apoptosis

JOURNAL ARTICLE published 2016 in Molecular Therapy - Methods & Clinical Development

Authors: Go Kagiya | Ryohei Ogawa | Fuminori Hyodo | Kei Yamashita | Mizuki Nakamura | Ayumi Ishii | Yukihiko Sejimo | Shintaro Tominaga | Masaharu Murata | Yoshikazu Tanaka | Masanori Hatashita

https://doi.org/10.1038/mtm.2016.9 Actions

Tumor antigen-loaded AAV vaccine drives protective immunity in a melanoma animal model

JOURNAL ARTICLE published March 2023 in Molecular Therapy - Methods & Clinical Development

Authors: Karina Krotova | Hisae Kuoch (Yoshitomi) | Colin Caine | George Aslanidi

https://doi.org/10.1016/j.omtm.2023.01.006 Actions

AAV vector production: Troublesome host innate responses in another setting

JOURNAL ARTICLE published March 2023 in Molecular Therapy - Methods & Clinical Development

Authors: J. Fraser Wright

https://doi.org/10.1016/j.omtm.2023.02.008 Actions

Clodronate Improves Survival of Transplanted Hoxb8 Myeloid Progenitors with Constitutively Active GMCSFR in Immunocompetent Mice

JOURNAL ARTICLE published December 2017 in Molecular Therapy - Methods & Clinical Development

Research funded by NIH/NCI (R21CA182703)

Authors: Simon Lee | Saul Kivimäe | Francis C. Szoka

https://doi.org/10.1016/j.omtm.2017.08.007 Actions

AUF1 gene transfer increases exercise performance and improves skeletal muscle deficit in adult mice

JOURNAL ARTICLE published September 2021 in Molecular Therapy - Methods & Clinical Development

Research funded by National Institutes of Health (UL1 TR00038) | National Institute of Arthritis and Musculoskeletal and Skin Diseases (1R01 AR074430-01)

Authors: Dounia Abbadi | John J. Andrews | Olga Katsara | Robert J. Schneider

https://doi.org/10.1016/j.omtm.2021.07.005 Actions

The Clonal Fate of Live Cells

JOURNAL ARTICLE published June 2017 in Molecular Therapy - Methods & Clinical Development

Authors: Wei Wang | Raffaele Fronza | Manfred Schmidt

https://doi.org/10.1016/j.omtm.2017.03.007 Actions

DNAJC14 Ameliorates Inner Ear Degeneration in the DFNB4 Mouse Model

JOURNAL ARTICLE published June 2020 in Molecular Therapy - Methods & Clinical Development

Research funded by Ministry of Health & Welfare, Republic of Korea (HI16C0142) | National Research Foundation of Korea (2017R1D1A1B03030046,2016M3A9B5941215)

Authors: Hye Ji Choi | Hyun Jae Lee | Jin Young Choi | Ik Hyun Jeon | Byunghwa Noh | Sushil Devkota | Han-Woong Lee | Seong Kug Eo | Jae Young Choi | Min Goo Lee | Jinsei Jung

https://doi.org/10.1016/j.omtm.2019.11.019 Actions

Engineering new metabolic pathways in isolated cells for the degradation of guanidinoacetic acid and simultaneous production of creatine

JOURNAL ARTICLE published June 2022 in Molecular Therapy - Methods & Clinical Development

Authors: Marzia Bianchi | Luigia Rossi | Francesca Pierigè | Pietro De Angeli | Mattia Paolo Aliano | Claudia Carducci | Emanuele Di Carlo | Tiziana Pascucci | Francesca Nardecchia | Vincenzo Leuzzi | Mauro Magnani

https://doi.org/10.1016/j.omtm.2022.02.007 Actions

Genetically Corrected iPSC-Derived Neural Stem Cell Grafts Deliver Enzyme Replacement to Affect CNS Disease in Sanfilippo B Mice

JOURNAL ARTICLE published September 2018 in Molecular Therapy - Methods & Clinical Development

Research funded by National Institute of Neurological Disorders and Stroke (1R41NS092221-0181,5T32 GM8243-28,R21NS096044,1R01 NS088766)

Authors: Don Clarke | Yewande Pearse | Shih-hsin Kan | Steven Q. Le | Valentina Sanghez | Jonathan D. Cooper | Patricia I. Dickson | Michelina Iacovino

https://doi.org/10.1016/j.omtm.2018.06.005 Actions

The human ankyrin 1 promoter insulator sustains gene expression in a β-globin lentiviral vector in hematopoietic stem cells

JOURNAL ARTICLE published 2015 in Molecular Therapy - Methods & Clinical Development

Authors: Zulema Romero | Beatriz Campo-Fernandez | Jennifer Wherley | Michael L Kaufman | Fabrizia Urbinati | Aaron R Cooper | Megan D Hoban | Kismet M Baldwin | Dianne Lumaquin | Xiaoyan Wang | Shantha Senadheera | Roger P Hollis | Donald B Kohn

https://doi.org/10.1038/mtm.2015.12 Actions

PGE2 and Poloxamer Synperonic F108 Enhance Transduction of Human HSPCs with a β-Globin Lentiviral Vector

JOURNAL ARTICLE published June 2019 in Molecular Therapy - Methods & Clinical Development

Research funded by California Institute for Regenerative Medicine (DR3-06945) | T32 Medical Scientist Training Program (T32GM008042)

Authors: Katelyn E. Masiuk | Ruixue Zhang | Kyle Osborne | Roger P. Hollis | Beatriz Campo-Fernandez | Donald B. Kohn

https://doi.org/10.1016/j.omtm.2019.03.005 Actions

Adipose Mesenchymal Cells-Derived EVs Alleviate DOCA-Salt-Induced Hypertension by Promoting Cardio-Renal Protection

JOURNAL ARTICLE published March 2020 in Molecular Therapy - Methods & Clinical Development

Research funded by National Institute of Science and Technology for Regenerative Medicine REGENERA (465656/2014-5) | Brazilian National Research Council (421916/2016-8,404092/2012-8,457222/2013-1,403151/2015-5,307605/2015-9) | Carlos Filho Rio de Janeiro State Research Foundation (E-26/201.142/2014,E-26/010.001283/2015)

Authors: Rafael Soares Lindoso | Jarlene Alécia Lopes | Renata Binato | Eliana Abdelhay | Christina Maeda Takiya | Kildare Rocha de Miranda | Lucienne Silva Lara | Antonella Viola | Benedetta Bussolati | Adalberto Vieyra | Federica Collino

https://doi.org/10.1016/j.omtm.2019.11.002 Actions

Enhancement of recombinant adeno-associated virus activity by improved stoichiometry and homogeneity of capsid protein assembly

JOURNAL ARTICLE published December 2023 in Molecular Therapy - Methods & Clinical Development

Authors: Takayuki Onishi | Michika Nonaka | Takahiro Maruno | Yuki Yamaguchi | Mitsuko Fukuhara | Tetsuo Torisu | Masaharu Maeda | Susan Abbatiello | Anisha Haris | Keith Richardson | Kevin Giles | Steve Preece | Noriko Yamano-Adachi | Takeshi Omasa | Susumu Uchiyama

https://doi.org/10.1016/j.omtm.2023.101142 Actions

Medicaid coverage practices for approved gene and cell therapies: Existing barriers and proposed policy solutions

JOURNAL ARTICLE published June 2023 in Molecular Therapy - Methods & Clinical Development

Authors: Jeremy Allen | Diane Berry | Francesca Cook | Ashley Hume | Rayne Rouce | Anirudh Srirangam | Jennifer Wellman | Caitlin McCombs

https://doi.org/10.1016/j.omtm.2023.05.015 Actions

GMP Production and Scale-Up of Adherent Neural Stem Cells with a Quantum Cell Expansion System

JOURNAL ARTICLE published September 2018 in Molecular Therapy - Methods & Clinical Development

Research funded by NCI (P30CA033572)

Authors: Revathiswari Tirughana | Marianne Z. Metz | Zhongqi Li | Christine Hall | David Hsu | Jim Beltzer | Alexander J. Annala | Diana Oganesyan | Margarita Gutova | Karen S. Aboody

https://doi.org/10.1016/j.omtm.2018.05.006 Actions

Increasing CRISPR Efficiency and Measuring Its Specificity in HSPCs Using a Clinically Relevant System

JOURNAL ARTICLE published June 2020 in Molecular Therapy - Methods & Clinical Development

Research funded by European Research Council (755758)

Authors: Jenny Shapiro | Ortal Iancu | Ashley M. Jacobi | Matthew S. McNeill | Rolf Turk | Garrett R. Rettig | Ido Amit | Adi Tovin-Recht | Zohar Yakhini | Mark A. Behlke | Ayal Hendel

https://doi.org/10.1016/j.omtm.2020.04.027 Actions

Regeneration of Tumor-Antigen-Specific Cytotoxic T Lymphocytes from iPSCs Transduced with Exogenous TCR Genes

JOURNAL ARTICLE published December 2020 in Molecular Therapy - Methods & Clinical Development

Authors: Takuya Maeda | Seiji Nagano | Soki Kashima | Koji Terada | Yasutoshi Agata | Hiroshi Ichise | Manami Ohtaka | Mahito Nakanishi | Fumihiro Fujiki | Haruo Sugiyama | Toshio Kitawaki | Norimitsu Kadowaki | Akifumi Takaori-Kondo | Kyoko Masuda | Hiroshi Kawamoto

https://doi.org/10.1016/j.omtm.2020.09.011 Actions

Development and Optimization of a Hydrophobic Interaction Chromatography-Based Method of AAV Harvest, Capture, and Recovery

JOURNAL ARTICLE published December 2020 in Molecular Therapy - Methods & Clinical Development

Research funded by University College London (UCL 15/0552)

Authors: David J. McNally | Bryan A. Piras | Catherine M. Willis | Timothy D. Lockey | Michael M. Meagher

https://doi.org/10.1016/j.omtm.2020.09.015 Actions
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