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Showing results for ISSN matching 1525-0016

Gene-mediated Restoration of Normal Myofiber Elasticity in Dystrophic Muscles

JOURNAL ARTICLE published January 2009 in Molecular Therapy

Authors: Stefania Puttini | Małgorzata Lekka | Olivier M Dorchies | Damien Saugy | Tania Incitti | Urs T Ruegg | Irene Bozzoni | Andrzej J Kulik | Nicolas Mermod

https://doi.org/10.1038/mt.2008.239 Actions

Acetylcholine-secreting cells improve age-induced memory deficits

JOURNAL ARTICLE published July 2003 in Molecular Therapy

Authors: Heather Dickinson-Anson | Jürgen Winkler | Lisa J Fisher | Hong-Jun Song | Mu-ming Poo | Fred H Gage

https://doi.org/10.1016/s1525-0016(03)00145-x Actions

Small but Significant: Inter- and Intrapatient Variations in iPS Cell–based Disease Modeling

JOURNAL ARTICLE published January 2013 in Molecular Therapy

Authors: Malte Sgodda | Tobias Cantz

https://doi.org/10.1038/mt.2012.273 Actions

Targeting Vascular Injury Using Hantavirus-Pseudotyped Lentiviral Vectors

JOURNAL ARTICLE published April 2006 in Molecular Therapy

Authors: Zhong Qian | Makalah Haessler | Julio A. Lemos | Jody R. Arsenault | Jennifer E. Aguirre | James R. Gilbert | Russell P. Bowler | Frank Park

https://doi.org/10.1016/j.ymthe.2005.11.016 Actions

Advanced gene-editing strategy for epidermolysis bullosa simplex

JOURNAL ARTICLE published February 2024 in Molecular Therapy

Authors: Adam Sheriff | Joanna Jacków-Malinowska

https://doi.org/10.1016/j.ymthe.2024.01.017 Actions

Heat Shock Protein 27 as a New Therapeutic Target for Radiation Sensitization of Head and Neck Squamous Cell Carcinoma

JOURNAL ARTICLE published August 2009 in Molecular Therapy

Authors: Elie Hadchity | Marie-Thérèse Aloy | Christian Paulin | Emma Armandy | Emmanuel Watkin | Robert Rousson | Martin Gleave | Olivier Chapet | Claire Rodriguez-Lafrasse

https://doi.org/10.1038/mt.2009.90 Actions

A new immune pathway mediating AAV immune responses

JOURNAL ARTICLE published February 2024 in Molecular Therapy

Authors: Ying Kai Chan

https://doi.org/10.1016/j.ymthe.2024.01.013 Actions

Genetically modified ZIKA virus as a microRNA-sensitive oncolytic virus against central nervous system tumors

JOURNAL ARTICLE published February 2024 in Molecular Therapy

Authors: Gabriela Machado Novaes | Caroline Lima | Carla Longo | Pedro Henrique Machado | Thais Peron Silva | Giovanna Gonçalves de Oliveira Olberg | Diego Grando Módolo | Márcia Cristina Leite Pereira | Tiago Goss Santos | Mayana Zatz | David Lagares | Marcelo de Franco | Paulo Lee Ho | Harry Bulstrode | Oswaldo Keith Okamoto | Carolini Kaid

https://doi.org/10.1016/j.ymthe.2024.01.006 Actions

Dual targeting of CD19 and CD22 against B-ALL using a novel high-sensitivity aCD22 CAR

JOURNAL ARTICLE published February 2024 in Molecular Therapy

Authors: Evangelia Kokalaki | Biao Ma | Mathieu Ferrari | Thomas Grothier | Warren Hazelton | Somayya Manzoor | Eren Costu | Julia Taylor | Anna Bulek | Saket Srivastava | Isaac Gannon | Ram Jha | Rosalind Gealy | Lukas Stanczuk | Tatiana Rizou | Mathew Robson | Mohamed El-Kholy | Vania Baldan | Matteo Righi | James Sillibourne | Simon Thomas | Shimobi Onuoha | Shaun Cordoba | Martin Pule

https://doi.org/10.1016/j.ymthe.2023.12.006 Actions

Allele-specific CRISPR-Cas9 editing of dominant epidermolysis bullosa simplex in human epidermal stem cells

JOURNAL ARTICLE published February 2024 in Molecular Therapy

Research funded by Fondazione Telethon (GGP20088) | European Research Council (101019289)

Authors: C. Cattaneo | E. Enzo | L. De Rosa | L. Sercia | F. Consiglio | M. Forcato | S. Bicciato | A. Paiardini | G. Basso | E. Tagliafico | A. Paganelli | C. Fiorentini | C. Magnoni | M.C. Latella | M. De Luca

https://doi.org/10.1016/j.ymthe.2023.11.027 Actions

726. Clinical Trial of Recombinant Adenovirus-p53 (Gendicine) Combined with Radiotherapy in Nasopharyngeal Carcinoma Patients

JOURNAL ARTICLE published 2006 in Molecular Therapy

Authors: Shanwen Zhang | Shaowen Xiao | Yan Sun | Changqing Liu | Xing Su | Dongming Li | Gang Xu | Guangying Zhu | Bo Xu

https://doi.org/10.1016/j.ymthe.2006.08.806 Actions

294. Myeloablative Conditioning Is Required for Efficient Engraftment of Gene-Modified Cells and Prevention of Antibody Production Against Transgene Products in a Rhesus Stem Cell Gene Therapy Model

JOURNAL ARTICLE published May 2015 in Molecular Therapy

Authors: Naoya Uchida | R. Patrick Weitzel | Charlotte Platner | Josiah Ballantine | Aylin C. Bonifacino | Sandra D. Price | Allen E. Krouse | Mark E. Metzger | Robert E. Donahue | John F. Tisdale

https://doi.org/10.1016/s1525-0016(16)33903-x Actions

CANT1 lncRNA Triggers Efficient Therapeutic Efficacy by Correcting Aberrant lncing Cascade in Malignant Uveal Melanoma

JOURNAL ARTICLE published September 2023 in Molecular Therapy

Authors: Yue Xing | Xuyang Wen | Xia Ding | Jiayan Fan | Peiwei Chai | Renbing Jia | Shengfang Ge | Guanxiang Qian | He Zhang | Xianqun Fan

https://doi.org/10.1016/j.ymthe.2023.08.002 Actions

Stem Cell Gene Therapy for Fanconi Anemia: Report from the 1st International Fanconi Anemia Gene Therapy Working Group Meeting

JOURNAL ARTICLE published July 2011 in Molecular Therapy

Authors: Jakub Tolar | Jennifer E Adair | Michael Antoniou | Cynthia C Bartholomae | Pamela S Becker | Bruce R Blazar | Juan Bueren | Thomas Carroll | Marina Cavazzana-Calvo | D Wade Clapp | Robert Dalgleish | Anne Galy | H Bobby Gaspar | Helmut Hanenberg | Christof Von Kalle | Hans-Peter Kiem | Dirk Lindeman | Luigi Naldini | Susana Navarro | Raffaele Renella | Paula Rio | Julián Sevilla | Manfred Schmidt | Els Verhoeyen | John E Wagner | David A Williams | Adrian J Thrasher

https://doi.org/10.1038/mt.2011.78 Actions

669. Direct and Indirect Immune Suppressive Effects of High Hepatic Expression Direct Effective Reversal of Factor IX Inhibitors by AAV Gene Transfer

JOURNAL ARTICLE published May 2013 in Molecular Therapy

https://doi.org/10.1016/s1525-0016(16)35004-3 Actions

624. Adenovirus Delivered to Tumor Endothelium by Angio-Adenobodies

JOURNAL ARTICLE published May 2007 in Molecular Therapy

https://doi.org/10.1016/s1525-0016(16)44830-6 Actions

826. Novel AAV Serotypes Result in Efficient Photoreceptor Transduction

JOURNAL ARTICLE published May 2007 in Molecular Therapy

https://doi.org/10.1016/s1525-0016(16)45032-x Actions

338. Therapeutic Fetal Hemoglobin Production in Erythroid Progeny of Normal and ß-Thalassemic Human CD34+ Cells Using Lentiviral Vectors Encoding γ-Globin or shRNA To Down Modulate the Transcriptional Repressor BCL11A

JOURNAL ARTICLE published May 2010 in Molecular Therapy

https://doi.org/10.1016/s1525-0016(16)37779-6 Actions

158. Evaluating Huntington's Disease Therapeutics In Vivo Using a Sensitive Measure of Transcriptional Dysregulation

JOURNAL ARTICLE published May 2012 in Molecular Therapy

https://doi.org/10.1016/s1525-0016(16)35962-7 Actions

Research Highlights

JOURNAL ARTICLE published March 2012 in Molecular Therapy

https://doi.org/10.1038/mt.2012.17 Actions
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