Facet browsing currently unavailable
Page 1 of 21636 results
Sort by: relevance publication year
Gene-mediated Restoration of Normal Myofiber Elasticity in Dystrophic Muscles JOURNAL ARTICLE published January 2009 in Molecular Therapy |
Acetylcholine-secreting cells improve age-induced memory deficits JOURNAL ARTICLE published July 2003 in Molecular Therapy |
Small but Significant: Inter- and Intrapatient Variations in iPS Cell–based Disease Modeling JOURNAL ARTICLE published January 2013 in Molecular Therapy |
Targeting Vascular Injury Using Hantavirus-Pseudotyped Lentiviral Vectors JOURNAL ARTICLE published April 2006 in Molecular Therapy |
Advanced gene-editing strategy for epidermolysis bullosa simplex JOURNAL ARTICLE published February 2024 in Molecular Therapy |
Heat Shock Protein 27 as a New Therapeutic Target for Radiation Sensitization of Head and Neck Squamous Cell Carcinoma JOURNAL ARTICLE published August 2009 in Molecular Therapy |
A new immune pathway mediating AAV immune responses JOURNAL ARTICLE published February 2024 in Molecular Therapy |
Genetically modified ZIKA virus as a microRNA-sensitive oncolytic virus against central nervous system tumors JOURNAL ARTICLE published February 2024 in Molecular Therapy |
Dual targeting of CD19 and CD22 against B-ALL using a novel high-sensitivity aCD22 CAR JOURNAL ARTICLE published February 2024 in Molecular Therapy |
Allele-specific CRISPR-Cas9 editing of dominant epidermolysis bullosa simplex in human epidermal stem cells JOURNAL ARTICLE published February 2024 in Molecular Therapy Research funded by Fondazione Telethon (GGP20088) | European Research Council (101019289) |
726. Clinical Trial of Recombinant Adenovirus-p53 (Gendicine) Combined with Radiotherapy in Nasopharyngeal Carcinoma Patients JOURNAL ARTICLE published 2006 in Molecular Therapy |
294. Myeloablative Conditioning Is Required for Efficient Engraftment of Gene-Modified Cells and Prevention of Antibody Production Against Transgene Products in a Rhesus Stem Cell Gene Therapy Model JOURNAL ARTICLE published May 2015 in Molecular Therapy |
CANT1 lncRNA Triggers Efficient Therapeutic Efficacy by Correcting Aberrant lncing Cascade in Malignant Uveal Melanoma JOURNAL ARTICLE published September 2023 in Molecular Therapy |
Stem Cell Gene Therapy for Fanconi Anemia: Report from the 1st International Fanconi Anemia Gene Therapy Working Group Meeting JOURNAL ARTICLE published July 2011 in Molecular Therapy |
669. Direct and Indirect Immune Suppressive Effects of High Hepatic Expression Direct Effective Reversal of Factor IX Inhibitors by AAV Gene Transfer JOURNAL ARTICLE published May 2013 in Molecular Therapy |
624. Adenovirus Delivered to Tumor Endothelium by Angio-Adenobodies JOURNAL ARTICLE published May 2007 in Molecular Therapy |
826. Novel AAV Serotypes Result in Efficient Photoreceptor Transduction JOURNAL ARTICLE published May 2007 in Molecular Therapy |
338. Therapeutic Fetal Hemoglobin Production in Erythroid Progeny of Normal and ß-Thalassemic Human CD34+ Cells Using Lentiviral Vectors Encoding γ-Globin or shRNA To Down Modulate the Transcriptional Repressor BCL11A JOURNAL ARTICLE published May 2010 in Molecular Therapy |
158. Evaluating Huntington's Disease Therapeutics In Vivo Using a Sensitive Measure of Transcriptional Dysregulation JOURNAL ARTICLE published May 2012 in Molecular Therapy |
Research Highlights JOURNAL ARTICLE published March 2012 in Molecular Therapy |