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Circular siRNAs for Reducing Off-Target Effects and Enhancing Long-Term Gene Silencing in Cells and Mice

JOURNAL ARTICLE published March 2018 in Molecular Therapy - Nucleic Acids

Research funded by National Natural Science Foundation of China (21422201,21372018,21672015) | National Major Scientific and Technological Special Project for “Significant New Drugs Development” (2017ZX09303013)

Authors: Liangliang Zhang | Duanwei Liang | Changmai Chen | Yuan Wang | Gubu Amu | Jiali Yang | Lijia Yu | Ivan J. Dmochowski | Xinjing Tang

Novel Fas-TNFR chimeras that prevent Fas ligand-mediated kill and signal synergistically to enhance CAR T cell efficacy

JOURNAL ARTICLE published June 2023 in Molecular Therapy - Nucleic Acids

Authors: Callum McKenzie | Mohamed El-Kholy | Farhaan Parekh | Mathew Robson | Katarina Lamb | Christopher Allen | James Sillibourne | Shaun Cordoba | Simon Thomas | Martin Pule

Pharmacokinetics and Toxicity in Rats and Monkeys of coDbait: A Therapeutic Double-stranded DNA Oligonucleotide Conjugated to Cholesterol

JOURNAL ARTICLE published 2012 in Molecular Therapy - Nucleic Acids

Authors: Anne Schlegel | Cyril Buhler | Flavien Devun | Céline Agrario | Saïk Urien | François Lokiec | Jian-Sheng Sun | Marie Dutreix

Retraction Notice to: MicroRNA-140 Inhibits the Epithelial-Mesenchymal Transition and Metastasis in Colorectal Cancer

JOURNAL ARTICLE published December 2022 in Molecular Therapy - Nucleic Acids

Authors: Jiazhi Li | Kun Zou | Lihui Yu | Wenyue Zhao | Ying Lu | Jun Mao | Bo Wang | Lu Wang | Shujun Fan | Bo Song | Lianhong Li

Retraction Notice to: lncRNA GAS5 Inhibits Cell Migration and Invasion and Promotes Autophagy by Targeting miR-222-3p via the GAS5/PTEN-Signaling Pathway in CRC

JOURNAL ARTICLE published December 2022 in Molecular Therapy - Nucleic Acids

Authors: Lin Liu | Hai-Jiang Wang | Tao Meng | Cheng Lei | Xin-Hui Yang | Qi-San Wang | Bo Jin | Jin-Feng Zhu

Retraction Notice to: hsa_circ_001653 Implicates in the Development of Pancreatic Ductal Adenocarcinoma by Regulating MicroRNA-377-MediatedHOXC6 Axis

JOURNAL ARTICLE published December 2022 in Molecular Therapy - Nucleic Acids

Authors: Huijuan Shi | Hui Li | Tiantian Zhen | Yu Dong | Xiaojuan Pei | Xiangliang Zhang

HIF-1α or HOTTIP/CTCF Promotes Head and Neck Squamous Cell Carcinoma Progression and Drug Resistance by Targeting HOXA9

JOURNAL ARTICLE published June 2022 in Molecular Therapy - Nucleic Acids

Authors: Qiang Sun | Shuai-Yuan Zhang | Jun-Fang Zhao | Xin-Guang Han | Hai-Bin Wang | Ming-Lei Sun

Retraction Notice to: Growth Arrest-Specific Transcript 5 (GAS5) Exerts Important Roles on the Treatment of BM45 Cells of Liver Cirrhosis

JOURNAL ARTICLE published June 2022 in Molecular Therapy - Nucleic Acids

Authors: Xing Lu | Ming Jiang | Juan Tian | Wei Liu | Fan Wu | Lijuan Yu | Guohui Feng | Shan Zhong | Ying Xiang | Hua Wen

Retraction Notice to: Circular RNA Profiling Reveals Exosomal circ_0006156 as a Novel Biomarker in Papillary Thyroid Cancer

JOURNAL ARTICLE published June 2022 in Molecular Therapy - Nucleic Acids

Authors: Guojun Wu | Wenhong Zhou | Xiaohua Pan | Zhigang Sun | Yongjie Sun | Hao Xu | Peng Shi | Jiyu Li | Ling Gao | Xingsong Tian

Retraction Notice to: lncRNA MALAT1 Accelerates Wound Healing of Diabetic Mice Transfused with Modified Autologous Blood via the HIF-1α Signaling Pathway

JOURNAL ARTICLE published June 2022 in Molecular Therapy - Nucleic Acids

Authors: Xiao-Qian Liu | Li-Shuang Duan | Yong-Quan Chen | Xiao-Ju Jin | Na-Na Zhu | Xun Zhou | Han-Wei Wei | Lei Yin | Jian-Rong Guo

Retroviral Replicating Vector Delivery of miR-PDL1 Inhibits Immune Checkpoint PDL1 and Enhances Immune Responses In Vitro

JOURNAL ARTICLE published March 2017 in Molecular Therapy - Nucleic Acids

Research funded by NIH (U01-NS59821,R01-CA105171)

Authors: Amy H. Lin | Christopher G. Twitty | Ryan Burnett | Andrew Hofacre | Leah A. Mitchell | Fernando Lopez Espinoza | Harry E. Gruber | Douglas J. Jolly

Targeted Exon Skipping to Address “Leaky” Mutations in the Dystrophin Gene

JOURNAL ARTICLE published 2012 in Molecular Therapy - Nucleic Acids

Authors: Sue Fletcher | Carl F. Adkin | Penny Meloni | Brenda Wong | Francesco Muntoni | Ryszard Kole | Clayton Fragall | Kane Greer | Russell Johnsen | Steve D. Wilton

rAAV-delivered PTEN therapeutics for prostate cancer

JOURNAL ARTICLE published March 2022 in Molecular Therapy - Nucleic Acids

Research funded by National Natural Science Foundation of China (81702536,82070784) | Department of Science and Technology of Sichuan Province (22CXRC0166) | Sichuan University West China Hospital (ZYGD18011) | National Institutes of Health (1P01AI100263-01,4P01HL131471-02,R01HL097088,R01NS076991-01,UG3 HL147367-01)

Authors: Jianzhong Ai | Jia Li | Qin Su | Hong Ma | Qiang Wei | Hong Li | Guangping Gao

Protecting Pax6 3′ UTR from MicroRNA-7 Partially Restores PAX6 in Islets from an Aniridia Mouse Model

JOURNAL ARTICLE published December 2018 in Molecular Therapy - Nucleic Acids

Research funded by National Science Engineering Research Council (RGPIN 293181-2010)

Authors: Kevin Yongblah | Spencer C. Alford | Bridget C. Ryan | Robert L. Chow | Perry L. Howard

miR-379 mediates insulin resistance and obesity through impaired angiogenesis and adipogenesis regulated by ER stress

JOURNAL ARTICLE published December 2022 in Molecular Therapy - Nucleic Acids

Research funded by National Institutes of Health (R01 DK065073,R01 DK081705,R01 HL106089) | National Cancer Institute (P30CA33572)

Authors: Maryam Abdollahi | Mitsuo Kato | Linda Lanting | Ragadeepthi Tunduguru | Mei Wang | Yangmeng Wang | Patrick T. Fueger | Qiong Wang | Wendong Huang | Rama Natarajan

hsa_circ_0001955 Enhances In Vitro Proliferation, Migration, and Invasion of HCC Cells through miR-145-5p/NRAS Axis

JOURNAL ARTICLE published December 2020 in Molecular Therapy - Nucleic Acids

Authors: Bisha Ding | Weimin Fan | Weiyang Lou

mitoTALEN reduces the mutant mtDNA load in neurons

JOURNAL ARTICLE published March 2024 in Molecular Therapy - Nucleic Acids

Authors: Sandra R. Bacman | Jose Domingo Barrera-Paez | Milena Pinto | Derek Van Booven | James B. Stewart | Anthony J. Griswold | Carlos T. Moraes

Dose-dependent Toxicity of Humanized Renilla reniformis GFP (hrGFP) Limits Its Utility as a Reporter Gene in Mouse Muscle

JOURNAL ARTICLE published 2013 in Molecular Therapy - Nucleic Acids

Authors: Lindsay M Wallace | Andrew Moreo | K Reed Clark | Scott Q Harper

Circular RNA circPSD3 alleviates hepatic fibrogenesis by regulating the miR-92b-3p/Smad7 axis

JOURNAL ARTICLE published March 2021 in Molecular Therapy - Nucleic Acids

Authors: Fang-tian Bu | Yan Zhu | Xin Chen | Ao Wang | Ya-fei Zhang | Hong-mei You | Yang Yang | Ya-ru Yang | Cheng Huang | Jun Li

Molecular Therapy's New Open-access Sibling

JOURNAL ARTICLE published 2012 in Molecular Therapy - Nucleic Acids

Authors: Robert M Frederickson | John J Rossi